Our MLD newborn screening efforts are now consolidated under a community-wide effort MLD Foundation is leading at:
Gene therapy is approved in Europe and will soon be reviewed by the FDA. There is additional pre-clinical work, and an enzyme replacement therapy clinical trial underway to provide very effective therapies to those newly diagnosed, but we all know that treating pre-symtomatically gives the best results. Newborn Screening is the key to early pre-symptomatic diagnostics and better outcomes.
• What is newborn screening?
• How do we get from a lab test to actually screening babies?
• Where does the RUSP and legislation fit in?
• How does your state/country implement a new screen?
• What can you do in your state, nationally, and globally?
The MLD Newborn Screening Academy™ is designed to answer these questions and more!
The format will be highly interactive and discussion based, especially as we get to the state-by-state and country-by-country implementation because each pubic health system is different so while the end goals of implementing a MLD screen are the same, the methods to get there will be varied.
The MLD Newborn Screening Academy will again havea dedicated session at the upcoming MLD Family Conference™, which will be available to everyone by live-stream and recorded video.